Genome Editing in Stem Cells
Tejwani L, Trujillo C, Thomas C, Muotri A. Genome Editing in Stem Cells. 2016, 287-309. DOI: 10.1007/978-3-319-30582-0_17.Peer-Reviewed Original ResearchGenome editingCRISPR/Cas9 systemPost-transcriptional levelPotential genetic therapyWild-type formStudy of geneticsGene functionGenetic functionsHuman genomeDeleterious mutationsParticular genesReverse geneticsCRISPR/Cas9 systemCellular phenomenaGenomeMolecular biologyCellular levelStem cellsEase of programmabilityMonogenic diseasesGenesEditingGeneticsSpecific modifications