Genome Editing Using CRISPR-Cas9 and Autoimmune Diseases: A Comprehensive Review
Lee M, Shin J, Yang J, Lee K, Cha H, Hong J, Park Y, Choi E, Tizaoui K, Koyanagi A, Jacob L, Park S, Kim J, Smith L. Genome Editing Using CRISPR-Cas9 and Autoimmune Diseases: A Comprehensive Review. International Journal Of Molecular Sciences 2022, 23: 1337. PMID: 35163260, PMCID: PMC8835887, DOI: 10.3390/ijms23031337.Peer-Reviewed Original ResearchConceptsProprotein convertase subtilisin/kexin type 9Systemic lupus erythematosusAutoimmune diseasesInflammatory bowel diseaseLowering low-density lipoprotein cholesterolBlock proprotein convertase subtilisin/kexin type 9Rheumatoid arthritisLow-density lipoprotein cholesterolTreatment of autoimmune diseasesManagement of autoimmune diseasesMultiple sclerosisType 1 diabetes mellitusBody's own tissuesPolymorphisms of multiple genesGene therapyLupus erythematosusLipoprotein cholesterolOrnithine transcarbamylaseHereditary tyrosinemiaRare diseaseType 9Animal modelsCRISPR-Cas9 treatmentBowel diseaseCRISPR-Cas9
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