154VP Usage of disease modifying therapies in spinal muscular atrophy and existing disparities: a population-based study from the MDA MOVR database
McLaren N, Joo D, Nowak R, Roy B. 154VP Usage of disease modifying therapies in spinal muscular atrophy and existing disparities: a population-based study from the MDA MOVR database. Neuromuscular Disorders 2024, 43: 104441.589. DOI: 10.1016/j.nmd.2024.07.598.Peer-Reviewed Original ResearchDisease modifying therapiesSpinal muscular atrophySurvival motor neuron 1Muscular Dystrophy AssociationModifying therapiesMuscular atrophyWhite Caucasian patientsSpinal muscular atrophy typesType 1 SMAType 2 SMALife saving therapyAlpha motor neuronsPopulation-based studyGroup of inherited neurodegenerative disordersCaucasian patientsZolgensmaNeuron 1Type 3 SMASpinal cordMuscle atrophyNusinersenPatientsTherapyMotor neuronsRisdiplam
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