2022
Therapies for lysosomal storage diseases: Principles, practice, and prospects for refinements based on evolving science
Grabowski GA, Mistry PK. Therapies for lysosomal storage diseases: Principles, practice, and prospects for refinements based on evolving science. Molecular Genetics And Metabolism 2022, 137: 81-91. PMID: 35933791, DOI: 10.1016/j.ymgme.2022.07.014.Peer-Reviewed Original Research
2016
Overcoming the Next Barriers to Successful Therapy.
Cohen IJ, Baris H, Mistry PK, Sands MS. Overcoming the Next Barriers to Successful Therapy. Pediatric Endocrinology Reviews : PER 2016, 13 Suppl 1: 629. PMID: 27491209.Peer-Reviewed Original Research