2024
Transporting randomized trial results to estimate counterfactual survival functions in target populations
Cao Z, Cho Y, Li F. Transporting randomized trial results to estimate counterfactual survival functions in target populations. Pharmaceutical Statistics 2024, 23: 442-465. PMID: 38233102, DOI: 10.1002/pst.2354.Peer-Reviewed Original ResearchSurvival functionFinite-sample performanceSample average treatment effectApproximate variance estimatorsIncorrect model specificationAverage treatment effectRight censoringDistributions of treatment effect modifiersVariance estimationInverse probability weightingSimulation studyRobust estimationComplex surveysAverage treatmentProbability weightingTreatment effect modifiersEstimationTreatment effectsModel specificationCensoringTarget populationDifferential distributionSurvey weightsEffect modifiersFunction
2018
Posterior Predictive $p$-Values with Fisher Randomization Tests in Noncompliance Settings: Test Statistics vs Discrepancy Measures
Forastiere L, Mealli F, Miratrix L. Posterior Predictive $p$-Values with Fisher Randomization Tests in Noncompliance Settings: Test Statistics vs Discrepancy Measures. Bayesian Analysis 2018, 13 DOI: 10.1214/17-ba1062.Peer-Reviewed Original ResearchDiscrepancy measureClassical test statisticsTest statisticIncorrect model specificationPosterior credible intervalsPosterior distributionFisher randomization testModel misspecificationCompliance typeImputation stepAverage causal effectCredible intervalsPermutation testComplier average causal effectGeneral schemeAdditional modelingModel specificationStatisticsRandomization testMisspecificationDifferent approachesOverall approachSchemeValidityRandomized experiments
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