Diseases of the Endocrine System | Genetics - Adult, Phase I-II

A Phase I/II Study of VTX-801 in Adult Patients With Wilson's Disease (GATEWAY)

Volunteers
Health Professionals

What is the purpose of this trial?

The objectives of this clinical trial are to assess, for up to 5 years, the safety, tolerability and pharmacological activity of a single ascending doses of VTX-801, a gene therapy, administered intravenously (IV) to adult patients with Wilson's Disease prior to and following background WD therapy withdrawal.

Trial with
Vivet Therapeutics, SAS
Ages
18 years - 60 years
Gender
Both

Find out more about who can participate in this trial

Contact Information

For more information about this study, including how to volunteer, contact Daksshi Hettiarachchi

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You can help our team find trials you might be eligible for by creating a volunteer profile in MyChart. To get started, create a volunteer profile, or contact helpusdiscover@yale.edu, or call 877.978.8343 for more information.

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Principal Investigator

Michael Schilsky, MD
Professor of Medicine; Medical Director, Adult Liver Transplant, Yale New Haven Transplantation Center

Sub-Investigators

Last Updated
04/18/2024
Study HIC
#2000028887