Examining Consistency Across NICE Single Technology Appraisals: A Review of Appraisals for Paroxysmal Nocturnal Haemoglobinuria
Donoghue J, Youngs M, Reeve A, Vydyula K, Kunst N, Trikha R, Gallacher D. Examining Consistency Across NICE Single Technology Appraisals: A Review of Appraisals for Paroxysmal Nocturnal Haemoglobinuria. PharmacoEconomics 2025, 1-10. PMID: 39934600, DOI: 10.1007/s40273-025-01472-5.Peer-Reviewed Original ResearchSingle Technology AppraisalNational Institute for Health and Care ExcellenceTechnology appraisalCost-effectiveness evidenceParoxysmal nocturnal haemoglobinuriaEconomic modelExamination consistAppraisalCare ExcellenceHealth technologiesFollow-up lengthImplementation of health technologyIndirect comparisonsDose escalationCost-effective healthcareEvidenceClinical evidencePositive recommendations
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