2025
Examining Consistency Across NICE Single Technology Appraisals: A Review of Appraisals for Paroxysmal Nocturnal Haemoglobinuria
Donoghue J, Youngs M, Reeve A, Vydyula K, Kunst N, Trikha R, Gallacher D. Examining Consistency Across NICE Single Technology Appraisals: A Review of Appraisals for Paroxysmal Nocturnal Haemoglobinuria. PharmacoEconomics 2025, 1-10. PMID: 39934600, DOI: 10.1007/s40273-025-01472-5.Peer-Reviewed Original ResearchSingle Technology AppraisalNational Institute for Health and Care ExcellenceTechnology appraisalCost-effectiveness evidenceParoxysmal nocturnal haemoglobinuriaEconomic modelExamination consistAppraisalCare ExcellenceHealth technologiesFollow-up lengthImplementation of health technologyIndirect comparisonsDose escalationCost-effective healthcareEvidenceClinical evidencePositive recommendations
2020
Calculating the Expected Value of Sample Information in Practice: Considerations from 3 Case Studies
Heath A, Kunst N, Jackson C, Strong M, Alarid-Escudero F, Goldhaber-Fiebert JD, Baio G, Menzies NA, Jalal H. Calculating the Expected Value of Sample Information in Practice: Considerations from 3 Case Studies. Medical Decision Making 2020, 40: 314-326. PMID: 32297840, PMCID: PMC7968749, DOI: 10.1177/0272989x20912402.Peer-Reviewed Original ResearchConceptsHealth economic modelApproximation methodEconomic modelTraditional Monte Carlo methodTraditional Monte CarloMonte Carlo algorithmMonte Carlo methodHigh computational burdenSample informationCarlo algorithmData generation processCarlo methodMonte CarloComputational burdenComputational speedPolicy decisionsComplex decision modelsComputation methodDecision modelRealistic exampleSample sizeEVSIDifferent examplesExpected valuesCarlo
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