Genetics Department Seminar Series: "Gene Delivery Strategies: From Viruses to Lipid Nanoparticles"

Novel gene therapy treatments and engineered gene editing tools, such as CRISPR, have begun to show success and hold great promise for treating a large number of inherited diseases but the major challenge of delivery still remains. My talk will focus on my work on viral delivery strategies for the retina and novel lipid nanoparticle systems.